Recent advances in somatic gene therapy for hereditary respiratory diseases.
نویسندگان
چکیده
منابع مشابه
Recent Advances in Hemophilia Gene Therapy
Heterogeneous loss of function mutations at F8 and F9 genes causes X-linked recessive bleeding disorders, hemophilia A (HA) and hemophilia B (HB), respectively. HA is clinically indistinguishable from HB and accounts for more than 80% of hemophilia cases; the former affects 1/5000 and the latter 1/25000 male births worldwide. In Iran, it is estimated that around 4300 HA and 900 HB patients are ...
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ژورنال
عنوان ژورنال: Thorax
سال: 1992
ISSN: 0040-6376
DOI: 10.1136/thx.47.4.315